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Anakinra in Sanfilippo syndrome: a phase 1/2 trial

Medicine and Health

Anakinra in Sanfilippo syndrome: a phase 1/2 trial

L. E. Polgreen, A. H. Chen, et al.

This phase 1/2 trial conducted by Lynda E. Polgreen and colleagues explored the benefits of anakinra, an interleukin-1 receptor antagonist, on patients with Sanfilippo syndrome, showing promise in improving neurobehavioral and functional outcomes while maintaining safety.... show more
Citation Metrics
Citations
7
Influential Citations
1
Reference Count
53
Citation by Year

Note: The citation metrics presented here have been sourced from Semantic Scholar and OpenAlex.

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